Project Title: Lentiviral-mediated gene transfer of TCIRG1 to correct osteoclast function in autosomal recessive osteopetrosis.
Sara Penna

Project Title: Lentiviral-mediated gene transfer of TCIRG1 to correct osteoclast function in autosomal recessive osteopetrosis.
Project Title: Improving targeted gene editing in hematopoietic stem cells for clinical translation